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3D Illustration Helix DNA molecule with modified genes. Correcting mutation by genetic engineering. Concept Molecular genetics.

Novel genome editing strategy to treat genetic disorders

Start date project: 2023
Involved institutes: LUMC
Stage: Preclinical
Status: Ongoing

Gene Therapy for X-linked agammaglobulinemia (XLA)

AAV Stealth switch for applications in gene therapy

Start date project: 2022
Involved institutes: LUMC, KNAW
Stage: Preclinical
Status: Ongoing

AAV Stealth switch for applications in gene therapy

Establishment of a clinical grade human iPS cell line

Start project: 2020
Involved institutes: LUMC, NECSTGEN
Stage: Preclinical
Status: Ongoing

Drug discovery tools

Reversibly Immortalizable Cardiomyocytes

Start date project: 2018
Involved institutes: LUMC
Status: Ongoing