![3D Illustration Helix DNA molecule with modified genes. Correcting mutation by genetic engineering. Concept Molecular genetics.](https://www.starfishinnovations.com/wp-admin/admin-ajax.php?action=kernel&p=image&src=%7B%22file%22%3A%22wp-content%2Fuploads%2F2020%2F12%2Fbigstock-221731816.jpg%22%2C%22thumbnail%22%3A%22445%2C%2C%22%7D&hash=c2f05ce2)
Novel genome editing strategy to treat genetic disorders
Start date project: 2023
Involved institutes: LUMC
Stage: Preclinical
Status: Ongoing
![Gene Therapy for X-linked agammaglobulinemia (XLA)](https://www.starfishinnovations.com/wp-admin/admin-ajax.php?action=kernel&p=image&src=%7B%22file%22%3A%22wp-content%2Fuploads%2F2020%2F11%2Fbigstock-Body-cells-under-a-microscope-375721339.jpg%22%2C%22thumbnail%22%3A%22445%2C%2C%22%7D&hash=3aed1650)
AAV Stealth switch for applications in gene therapy
Start date project: 2022
Involved institutes: LUMC, KNAW
Stage: Preclinical
Status: Ongoing
![AAV Stealth switch for applications in gene therapy](https://www.starfishinnovations.com/wp-admin/admin-ajax.php?action=kernel&p=image&src=%7B%22file%22%3A%22wp-content%2Fuploads%2F2020%2F11%2Fbigstock-Body-cells-under-a-microscope-375736255.jpg%22%2C%22thumbnail%22%3A%22445%2C%2C%22%7D&hash=aebfb460)
Establishment of a clinical grade human iPS cell line
Start project: 2020
Involved institutes: LUMC, NECSTGEN
Stage: Preclinical
Status: Ongoing
![Drug discovery tools](https://www.starfishinnovations.com/wp-admin/admin-ajax.php?action=kernel&p=image&src=%7B%22file%22%3A%22wp-content%2Fuploads%2F2020%2F11%2Fbigstock-The-Development-Of-New-Drugs-F-376276789.jpg%22%2C%22thumbnail%22%3A%22445%2C%2C%22%7D&hash=408390b6)
Reversibly Immortalizable Cardiomyocytes
Start date project: 2018
Involved institutes: LUMC
Status: Ongoing